Rare Premature Aging Disease Successfully Treated with Farnesyltransferase Inhibitor, JAMA Small Observational Study

Small cohort of children with rare progeria Hutchinson-Gilford syndrome showed dramatically lower mortality when given lonafarnib than untreated patients.

Source: Association of Lonafarnib Treatment vs No Treatment With Mortality Rate in Patients With Hutchinson-Gilford Progeria Syndrome | Pediatrics | JAMA | JAMA Network